Babies diagnosed with Spinal Muscular Atrophy at birth who received life-changing gene therapy are now living longer and healthier, celebrating their first birthday symptom-free or with minimal symptoms thanks to the ground-breaking research by Kids Research.

New trial investigates the occurrence of food allergies in children amid dramatic rise in the number of children diagnosed with food allergies.

At four months of age Sophia is reaching all her developmental milestones. She demonstrates good head control while sitting supported and can even roll from her tummy to her back.

New study found fenfluramine was an effective and safe treatment for Dravet Syndrome, reducing the number of epileptic seizures by over 75 per cent. For Bronte, this meant she went from having 10 seizures a day to just one or two a week and even began having seizure free weeks.

In a new clinical trial being led by The Children’s Hospital at Westmead, doctors are testing whether drug used to help adult Alzheimer’s patients can help improve some of the devastating features of Rett syndrome.